New Potential Treatment for Muscular Dystrophy Appears to Be Safe

Myostatin, a protein that blocks muscle growth, has shown promising results as a potential therapeutic target for treating muscular dystrophy in animal studies, where its inhibition led to increased muscle mass and strength. A new study, the first to evaluate a myostatin inhibitor in patients, assessed its safety in adults with muscular dystrophy and found that it was well-tolerated. The study was published today in Annals of Neurology, the official journal of the American Neurological Association.